Efficacy of sapropterin dihydrochloride (tetrahydrobiopterin, 6R-BH4) for reduction of phenylalanine concentration in patients with phenylketonuria: a phase III randomised placebo-controlled study
Titel:
Efficacy of sapropterin dihydrochloride (tetrahydrobiopterin, 6R-BH4) for reduction of phenylalanine concentration in patients with phenylketonuria: a phase III randomised placebo-controlled study
Auteur:
Levy, Harvey L Milanowski, Andrzej Chakrapani, Anupam Cleary, Maureen Lee, Philip Trefz, Friedrich K Whitley, Chester B Feillet, François Feigenbaum, Annette S Bebchuk, Judith D Christ-Schmidt, Heidi Dorenbaum, Alex